FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

Three men with late-onset spinal muscular atrophy (SMA) on Evrysdi treatment were able to conceive with their partners, per a ...

Affordable generic version of SMA drug Risdiplam soon available in India, offering hope to patients and activists.

Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC Graduate and Professional Council.

Thiruvananthapuram: Health minister Veena George announced the launch of the Vishu Kaineettam project, aimed at supporting ...

The Supreme Court of India seeks responses from the Centre and Roche on making the spinal muscular atrophy treatment drug ...

It's that time of year when you can become a Hero for Hope and donate to ABC15's annual Telethon for Phoenix Children's ...

PTC Therapeutics, Inc.’s PTCT share price has surged by 6.72%, which has investors questioning if this is right time to sell.

The Supreme Court will review the Rs 50 lakh cap on the central government's aid for treating rare diseases like SMA. The ...

Supreme Court examines pleas challenging 50 lakh cap on Centre's assistance for treating rare diseases like SMA.