Two-year data with eyeDNA Therapeutics’ gene therapy for retinitis pigmentosa (RP), an inherited form of blindness, has prompted the biotech to seek discussions with regulators about the design ...

Nanoscope Therapeutics is on the brink of filing for FDA approval of what could be the first gene therapy for incurable eye disease retinitis pigmentosa (RP) that can be used regardless of ...

antibodies against both Dsg1 and Dsg3 are produced, resulting in involvement of both the skin and the mucous membranes. The mechanism of autoantibody production has yet to be elucidated.

Donald Trump called Ukrainian President Volodymyr Zelenskyy after speaking with Russian President Vladimir Putin, discussing ways to end the Russian invasion of Ukraine. Both Trump and Zelenskyy ...

Feb. 10, 2025 — Rapid weight loss affects muscle mass and can increase the risk of osteoporosis. But now there is good news for people taking weight loss medication who may be at risk. A new ...

Feb. 6, 2025 — Despite new medication, cystic fibrosis often leads to permanent lung damage. Researchers have discovered that the disease causes changes in the immune system early in life ...

The objective of this trial was to evaluate safety and tolerability and identify dose level for further evaluation.