Hemophilia is a genetic condition where the body doesn't produce enough of the clotting factors needed to stop bleeding. Know ...

By: Dr. Vijay Ramanan Haemophilia B constitutes a severe rare genetic bleeding condition which interferes strongly with blood ...

A couple whose son has a rare genetic skin condition say it is hard to process that a cuddle could "tear his skin". Twenty month old Albi was born with a severe form of recessive dystrophic ...

Are you looking for something different to do this coming summer? Well, why not take a trip out into the Finger Lakes region ...

In a new development, researchers have successfully created an efficient two-line system for hybrid seed production in ...

INmune Bio partners with UK-based Catapult to enhance cell therapy manufacturing for the production of its cell therapies.

INmune Bio (INMB) has partnered with the Cell and Gene Therapy Catapult to establish large-scale, commercial-ready manufacturing for its cell ...

Abeona Therapeutics faces a pivotal FDA decision after a CRL-led crash and partial rebound in pz-cel’s valuation. Check out ...

Lined up for the FDA in the coming weeks are a cell-based gene therapy for a rare skin disease and two product expansions for ...

Pharma announced the publication of a paper titled, “Phenotypic characterization of ENPP1 deficiency: generalized arterial ...

Me’s debacle should be a major wake-up call, reminding policymakers and all of us of the risks of giving access to our ...

Metachromatic leukodystrophy (MLD) is an autosomal recessive lysosomal storage disease originating from biallelic pathogenic variants in the ARSA gene, mainly affecting young children.