Spinal muscular atrophy (SMA) is a disorder affecting the motor neurons—nerve cells that control voluntary muscle movement. These cells are located in the spinal cord. Because the muscles cannot ...

A rare genetic condition, Spinal Muscular Atrophy (SMA) affects one in 7,000 people in India. It mostly affects children and often leads to infant mortality In a breakthrough for Spinal Muscular ...

The Mayo Clinic and Exact Sciences are developing an easy, noninvasive test to detect endometrial cancer in women with abnormal vaginal bleeding. It analyzes vaginal fluid collected on tampons for ...

The financing will help Character bring its two most advanced programs into clinical testing. One, dubbed CTX114, is being tested in geographic atrophy, a common eye condition and an advanced stage of ...

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several companies—including Novartis, Scholar Rock and Biogen—progressing novel candidates through ...