Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

Thiruvananthapuram: Health minister Veena George announced the launch of the Vishu Kaineettam project, aimed at supporting ...

The state govt provides free treatment to numerous children with rare diseases like Spinal Muscular Atrophy (SMA), growth ...

Scholar Rock Holding Corporation's apitegromab shows promise for SMA treatment, aims for 2025 launch. Click for my updated ...

PTC Therapeutics, Inc.’s PTCT share price has surged by 6.72%, which has investors questioning if this is right time to sell.

Learn more about whether Neurocrine Biosciences, Inc. or PTC Therapeutics, Inc. is a better investment based on AAII's A+ ...

Those with spinal muscular atrophy can get emotional support by building an SMA support system that includes SMA communities ...

The issues at Temple Street in a HIQA report published this week relate to a consultant, identified as Surgeon A, and ...

Three men with late-onset spinal muscular atrophy (SMA) on Evrysdi treatment were able to conceive with their partners, per a ...

Fibromyalgia does not have a cure, but treatments are available for the disease's musculoskeletal ... And, an expert in a crippling condition -- spinal muscular atrophy -- is enthusiastic about a ...

Meanwhile, Biogen is facing challenges elsewhere, notably with its stalled Alzheimer's therapy Aduhelm (aducanumab) and spinal muscular atrophy treatment Spinraza (nusinersen), which is seeing ...