Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

Affordable generic version of SMA drug Risdiplam soon available in India, offering hope to patients and activists.

22. Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation ...

The Supreme Court of India seeks responses from the Centre and Roche on making the spinal muscular atrophy treatment drug ...

for apitegromab for the improvement of motor function in patients with spinal muscular atrophy (SMA). Apitegromab, a fully human monoclonal antibody, works by selectively binding to the pro- and ...

Supreme Court examines pleas challenging 50 lakh cap on Centre's assistance for treating rare diseases like SMA.

The NIH is considering a catastrophic cut to indirect cost reimbursements for public universities, which would hurt the ...