The candidate is a systemically administered investigational AAV8 gene therapy that drives liver-specific ... and achieves hair follicle transfection. Last year, the anti-aging company also signed a ...

In this interview, News Med talks to Hinnah Campwala about the pivotal role of transfection in modern research and drug discovery. Transfection is a tool that sees widespread use across a diverse ...

GENV-HEM (AAV8.FVa) is a gene therapy for all hemophilias, including inhibitor patients, and without the durability issues that have plagued Factor VIII gene therapies. GENV-002 (AAV9.GAA and AAV9 ...

Fill out the form below and we'll send your colleague an invitation to the "Advanced Strategies for Effective mRNA Transfection in T Cells" event. Optimizing mRNA transfection in human T cells is a ...

A second pediatric patient was recently dosed, and the pediatric cohort is expected to complete enrollment in Q2 2025; initial data from all three patients anticipated in Q3 2025 FDA Type D ...

We further conducted in vitro and in vivo functional delivery of mRNA and found that the LNP fraction with the highest mRNA loading levels was the least transfection competent.

HEMLIBRA has strong market potential due to its unique, subcutaneous prophylactic treatment for Hemophilia A, including patients with and without factor VIII inhibitors. With increasing global ...