Thiruvananthapuram: Health minister Veena George announced the launch of the Vishu Kaineettam project, aimed at supporting ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

The state govt provides free treatment to numerous children with rare diseases like Spinal Muscular Atrophy (SMA), growth ...

Scholar Rock Holding Corporation's apitegromab shows promise for SMA treatment, aims for 2025 launch. Click for my updated ...

PTC Therapeutics, Inc.’s PTCT share price has surged by 6.72%, which has investors questioning if this is right time to sell.

Zolgensma is a prescription drug that’s used to treat spinal muscular atrophy (SMA) in young children. Zolgensma’s cost may depend on factors such as your child’s treatment plan and whether ...

Learn more about whether Ionis Pharmaceuticals, Inc. or Neurocrine Biosciences, Inc. is a better investment based on AAII's ...

Three men with late-onset spinal muscular atrophy (SMA) on Evrysdi treatment were able to conceive with their partners, per a ...

Those with spinal muscular atrophy can get emotional support by building an SMA support system that includes SMA communities ...

The company develops Apitegromab, an inhibitor of the activation of myostatin that is in Phase 3 clinical trial for the treatment of spinal muscular atrophy; and SRK-181, which has completed Phase ...

Meanwhile, Biogen is facing challenges elsewhere, notably with its stalled Alzheimer's therapy Aduhelm (aducanumab) and spinal muscular atrophy treatment Spinraza (nusinersen), which is seeing ...