A recent study involving researchers from the University of Basel reveals that slowing down the intracellular transport of ...

11-year-old Hunter Whisler is living with Duchenne Muscular Dystrophy, a rare and fatal disorder which leads to muscle degeneration and weakness. But Hunter’s grandmother, Susan Samuelson, said they ...

New consensus guidelines outline best practices for orthopedic management in Duchenne muscular dystrophy, focusing on ...

One visit to Virginia Peninsula Community College’s Historic Triangle Campus last summer eased any concerns they might have had. Soon after entering the building, Nicholas and his mother, Liz, were ...

The desperate parents of a disabled child are pleading with the NHS to give their son access to a new drug. Jessica and ...

Patients with life-limiting condition set to receive new treatment at Children's Hospital but those at Heartlands must wait ...

Although only living in the Berkshires for a few years, Evan Butts has already ingrained himself into the community. A server ...

Sarepta Therapeutics Inc. misled investors about the safety and prospects for one of its Duchenne muscular dystrophy ...

Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.

The FDA found that data from a single Phase II study were “insufficient” to justify an accelerated approval review for ...

Edgewise Therapeutics, Inc., a leading muscle disease biopharmaceutical company, unveiled positive results in its sevasemten programme for Becker and Duchenne muscular dystrophies. The company ...

Not too long ago, Editas Medicine was working on Reni-Cel, an investigational treatment for two rare blood disorders. Although the data from clinical trials for this medicine was promising, Editas ...